Remember "Baby KJ"? Now CRISPR pioneers have partnered with the Chan Zuckerberg Initiative to launch center for curing rare ...

India offers a treasure trove of genetic data for AI-enabled researchers to develop therapies neglected by commercial ...

A Ph.D. student in biomolecular engineering at the University of California, Santa Cruz, has built a software program ...

KJ Muldoon recently made history by becoming the first patient to receive a personalized CRISPR gene therapy, designed specifically for the genetic mutations causing his rare metabolic disease. | KJ ...

The organizations launched the center with a $20 million CZI grant to build on the success of the first personalized CRISPR base-editing therapy.

Personalized CRISPR cures for children born with rare genetic diseases are now a step closer to being more widely available.

In vivo base editing enables precise, single-nucleotide changes to DNA without double-strand breaks. A recent application in ...

Personalized CRISPR cures for children born with rare genetic diseases are now a step closer to being more widely available.

Rare genetic diseases are challenging for patients and their families—made all the more overwhelming because symptoms tend to ...

New research has found a novel target with therapeutic potential for metastatic eye melanoma—an aggressive eye cancer—with ...

Vertex Pharmaceuticals unveiled impressive long-term results for its CRISPR/Cas9 gene therapy, PrCASGEVY, at the EHA Congress ...