For decades, the dream of fixing harmful mutations in mitochondrial DNA felt out of reach. Scientists have long known these ...

An experimental treatment called VERVE-102 lowers the amount of "bad" cholesterol in the blood of people with specific cholesterol-raising conditions.

Amber Salzman, Ph.D., CEO at Epicrispr Biotechnologies, joined the Business of Biotech live in Boston to talk about ...

DNA makes RNA, RNA makes protein, protein makes phenotype—was the guiding framework for understanding inheritance and disease ...

Drought- and salt-resistant rice varieties are being developed in India as part of fascinating gene-editing work.

CZI and the IGI announce the funding of the Center for Pediatric CRISPR Cures to use CRISPR-based editing technology to advance cures.

A Ph.D. student in biomolecular engineering at the University of California, Santa Cruz, has built a software program ...

KJ Muldoon recently made history by becoming the first patient to receive a personalized CRISPR gene therapy, designed specifically for the genetic mutations causing his rare metabolic disease. | KJ ...

Personalized CRISPR cures for children born with rare genetic diseases are now a step closer to being more widely available.

Rare genetic diseases are challenging for patients and their families—made all the more overwhelming because symptoms tend to ...