New research has identified the enzyme glutamate dehydrogenase 1 (GLUD1) as a new therapeutic target for Duchenne muscular dystrophy (DMD). In preclinical DMD mouse models, investigators demonstrated ...

New research has identified the enzyme glutamate dehydrogenase 1 (GLUD1) as a new therapeutic target for Duchenne muscular dystrophy (DMD). In ...

With recent improvements in healthcare, individuals with Duchenne muscular dystrophy (DMD) have prolonged life expectancy, and it is therefore vital to preserve their independence. Hand function plays ...

The company said it was “surprised” by the decision, which followed the ouster of cell and gene therapy officials from the ...

TAS-205 showed no significant impact on motor function in patients with Duchenne muscular dystrophy (DMD), highlighting the ongoing search for effective treatments for the rare condition.

The FDA rejected a Duchenne muscular dystrophy cell therapy from Capricor Therapeutics, as a larger study of the treatment ...

Background Over the last 30 years, there has been little improvement in the age of diagnosis of Duchenne muscular dystrophy (DMD) (mean age of 4.5–4.11 years). Aim To review the diagnostic process for ...

A second Duchenne muscular dystrophy patient died after being treated with the gene therapy delandistrogene moxeparvovec (Elevidys), Sarepta Therapeutics said Sunday.

Physical activity and rehabilitation are key components of Duchenne muscular dystrophy treatment, despite recent drug therapy advances. "Rehabilitation care and rehabilitation teams with ...

Duchenne Muscular Dystrophy (DMD) Pathophysiology The pathophysiology of Duchenne muscular dystrophy (DMD) revolves around the lack of functional dystrophin, which results in a fragile, permeable cell ...

WILLIAMSBURG — Since Nicholas Bahl-Moore has Duchenne muscular dystrophy, he and his family had to consider accessibility factors when looking into colleges. One visit to Virginia Peninsula ...

Genetics Duchenne muscular dystrophy (DMD) is a genetic disorder caused by mutations in the DMD gene—located on the X chromosome and representing the largest known human gene with 2.4 million base ...